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Gene therapy

1-minute read

Gene therapy corrects genetic diseases. It may involve replacing faulty genes or introducing new genes to treat disease. Therapeutic gene therapy is still in its infancy and many of the ethical guidelines for its use are still being developed.

Follow the links below to find trusted information about gene therapy. 

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Last reviewed: April 2022

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Gene therapy for haemophilia - Haemophilia Foundation Australia

Information about gene therapy in haemophilia, including types of gene therapy, haemophilia and genes, how gene therapy works, what happens when you have gene therapy and are on a clinical trial and frequently asked questions.

Read more on Haemophilia Foundation Australia website

Targeted therapy - Cancer Council Victoria

Targeted therapy is a drug treatment that targets specific features of cancer cells to stop growth and spread.

Read more on Cancer Council Victoria website

Pharmacogenomic Tests - Pathology Tests Explained

Some of us respond differently to the same medications that we take, or we may experience different side-effects from drugs

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Phenylketonuria (PKU) - Better Health Channel

PKU is an inherited disorder that prevents the normal breakdown of a protein found in some foods.

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Rare Cancers Australia - Research

MoST is a two part research program with the aim of treating as many patients as possible with personalised therapies

Read more on Rare Cancers Australia website

Genetic testing for cancer information | myVMC

Inherited genetic mutations increase the risk of certain cancers. Genetic testing is used to group cancers and develop new targeted cancer therapies.

Read more on myVMC – Virtual Medical Centre website

Neglected cancers | Garvan Institute of Medical Research

Read about rare or uncommon cancers, risks and treatment, real life stories, and Garvan's recent advances. Our clinical trials use genomic sequencing to aid prognosis and identify precision therapies.

Read more on Garvan Institute of Medical Research website

RAS gene mutation - Pathology Tests Explained

When, why and how the RAS gene mutation test is done

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PDGFRA-FIP1L1 gene rearrangement - Pathology Tests Explained

Why, when and how the PDGFRA-FIL1L1 gene rearrangement test is done.

Read more on Pathology Tests Explained website

ALK Mutation (Gene Rearrangement) - Pathology Tests Explained

When, why & how ALK Mutation testing is carried out

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